SES AUA 2025: PSA Dynamics from the Phase 3 EMBARK Trial: A Post Hoc Analysis

(UroToday.com) The 2025 SESAUA annual meeting featured a prostate cancer session and a presentation by Dr. Paul Sieber discussing a post hoc analysis from the phase 3 EMBARK study assessing PSA dynamics. FDA approval of enzalutamide for treatment of non-metastatic CSPC with biochemical recurrence at high risk for metastasis, was based on data from the EMBARK trial.


This was a phase 3 trial that demonstrated that enzalutamide + leuprolide (enzalutamide combination) and enzalutamide monotherapy significantly improved metastasis-free survival versus placebo + leuprolide alone in high-risk biochemically recurrent prostate cancer patients.1 EMBARK included a treatment suspension at week 37 if PSA was <0.2 ng/mL and re-initiation at pre-defined PSA thresholds. This post hoc analysis of PSA dynamics in EMBARK aimed to understand the time course to undetectable PSA and likelihood of undetectable PSA after treatment re-initiation.

EMBARK enrolled high-risk biochemically recurrent patients, post definitive therapy. High-risk was defined as PSA doubling time ≤9 months and PSA ≥2 ng/mL above nadir post radiotherapy or ≥1 ng/mL post radical prostatectomy ± postoperative radiotherapy. Patients were randomized (1:1:1) to receive enzalutamide combination 160 mg/day (double blind), leuprolide alone (double blind), or enzalutamide monotherapy (open label). Leuprolide 22.5 mg was administered every 12 weeks:
If serum PSA was <0.2 ng/mL at week 36, treatment was suspended at week 37 and restarted when PSA was ≥2 ng/mL for radical prostatectomy patients and ≥5 ng/mL for non-radical prostatectomy patients. A post hoc analysis of PSA dynamics was conducted in each treatment cohort.

The patient disposition based on treatment suspension status is highlighted in the following table:The patient disposition based on treatment suspension status is highlighted in the following table
Of 1,068 eligible patients, most in all three treatment groups reached undetectable PSA (<0.2 ng/mL) by week 25, with percentages higher for enzalutamide combination and monotherapy versus leuprolide alone:
Of 1,068 eligible patients, most in all three treatment groups reached undetectable PSA (<0.2 ng/mL) by week 25, with percentages higher for enzalutamide combination and monotherapy versus leuprolide alone
More patients had treatment suspended with enzalutamide combination and monotherapy versus leuprolide alone. Of patients who suspended treatment at week 37, 89% reinitiated treatment with enzalutamide monotherapy, 85% with leuprolide alone, and 75% with enzalutamide combination. Of patients who reinitiated treatment, 96% of men treated with enzalutamide combination and 90% treated with enzalutamide monotherapy reached undetectable PSA again versus 73% with leuprolide alone:More patients had treatment suspended with enzalutamide combination and monotherapy versus leuprolide alone. Of patients who suspended treatment at week 37, 89% reinitiated treatment with enzalutamide monotherapy, 85% with leuprolide alone, and 75% with enzalutamide combination. Of patients who reinitiated treatment, 96% of men treated with enzalutamide combination and 90% treated with enzalutamide monotherapy reached undetectable PSA again versus 73% with leuprolide alone
Metastasis free survival for patients who achieved or did not achieve undetectable PSA levels after treatment re-initiation is highlighted in the following figure:image-4.jpg
Dr. Sieber concluded his presentation discussing a post hoc analysis from the phase 3 EMBARK study assessing PSA dynamics with the following take-home points:

  • In patients with high-risk biochemical recurrence, more patients treated with enzalutamide (both as combination and monotherapy) versus leuprolide alone achieved:
    • Undetectable PSA levels at week 36 and subsequent treatment suspension at week 37
    • Undetectable PSA levels earlier (week ≤25)
    • Undetectable PSA levels after treatment re-initiation
  • Due to durable undetectable PSA levels (<0.2 ng/mL), more patients had treatment suspension ongoing in the enzalutamide combination group versus leuprolide alone after a median of 4 years 11 months
  • Independent of treatment type, achievement of undetectable PSA levels after treatment re-initiation was associated with improved metastasis free survival

Presented by: Paul R. Sieber, MD, Keystone Urology Specialists, Lancaster, PA

Written by: Zachary Klaassen, MD, MSc – Urologic Oncologist, Associate Professor of Urology, Georgia Cancer Center, Wellstar MCG Health, @zklaassen_md on Twitter during the Southeastern Section of the American Urological Association (SESAUA) 2025 Annual Meeting, Nashville, TN, Wed, Mar 12 – Sat, Mar 15, 2025.

References:

  1. Freedland SJ, de Almeida Luz M, De Giorgi U, et al. Improved Outcomes with Enzalutamide in Biochemically Recurrent Prostate Cancer. N Engl J Med 2023 Oct 19;389(16):1453-1465.